founders, Board of directors
Founded by scientists who are driven to find treatments for rare neuromuscular diseases our research, drug programs and commercial efforts are all guided by science & the practice of evidence based translational development of our therapeutic strategies.
Our goal is to develop the worlds first gene therapy to treat FSHD using novel patented CRISPRi technology.
There is currently no therapeutic treatment or cure for FSHD.
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Non exec Chair, Founder, Board Director